10-K – Annual report [Section 13 and 15(d), not S-K Item 405]

Aduro Biotech has filed a 10-K – Annual report [Section 13 and 15(d), not S-K Item 405] with the U.S. Securities and Exchange Commission (Filing, 10-K, Aduro Biotech, MAR 1, 2017, View Source [SID1234517920]).

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10-K – Annual report [Section 13 and 15(d), not S-K Item 405]

Merrimack has filed a 10-K – Annual report [Section 13 and 15(d), not S-K Item 405] with the U.S. Securities and Exchange Commission (Filing, 10-K, Merrimack, MAR 1, 2017, View Source [SID1234517916]).

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Pacira Pharmaceuticals Reports 2016 Financial Results and Provides Business Update

On March 1, 2017 Pacira Pharmaceuticals, Inc. (NASDAQ:PCRX) reported financial results for 2016 and its outlook for 2017. The company is also announcing positive topline results for its Phase 4 study of EXPAREL in total knee arthroplasty, or TKA (Press release, Pacira Pharmaceuticals, MAR 1, 2017, View Source;p=RssLanding&cat=news&id=2250542 [SID1234517950]).

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"We made important progress in 2016 advancing our three-part EXPAREL growth strategy and setting the stage for continued success," said Dave Stack, chief executive officer and chairman of Pacira. "We have multiple, major milestones on track for 2017, including the positive topline results reported today from our Phase 4 study in TKA. Our collaboration with DePuy Synthes is off to a strong start and will allow us to maximize these important data and broaden the use of EXPAREL as an opioid-sparing solution for prolonged postsurgical pain relief."

Recent Highlights

Positive topline results for Phase 4 TKA study. Pacira reported that its Phase 4 study of EXPAREL in patients undergoing TKA has met its co-primary endpoints for postsurgical pain and opioid reduction. The study was a multicenter, randomized, double-blind, controlled, parallel group study comparing EXPAREL based local analgesia infiltration to standard bupivacaine based local analgesia infiltration each as part of a standard multimodal analgesic protocol. The co-primary efficacy endpoints were the area under the curve (AUC) of visual analog scale (VAS) pain intensity scores from 12 to 48 hours after surgery and total opioid consumption from zero to 48 hours after surgery. The EXPAREL group achieved a statistically significant reduction in AUC VAS scores compared to the group who did not receive EXPAREL (p=0.0381). In addition, patients who received EXPAREL consumed significantly fewer opioids than patients who did not receive EXPAREL during the 48 hours that followed surgery (p=0.0048). The company plans to report the statistical results for key secondary endpoints from this study in the coming weeks. Full results will be submitted for publication in a peer-reviewed medical journal.

Partnership with DePuy Synthes to maximize EXPAREL opportunity. In January 2017, the company announced a co-promotion agreement with DePuy Synthes to market and promote the use of EXPAREL for orthopedic procedures in the US market. The DePuy Synthes field representatives, specializing in joint reconstruction, spine, sports medicine and trauma, will expand the reach and frequency of EXPAREL education in hospital surgical suites and ambulatory surgery centers. DePuy Synthes will also include EXPAREL in the Orthopedic Episode of Care Approach, a comprehensive offering for health systems and surgeons. In addition to supporting DePuy Synthes, Pacira will focus on soft tissue surgeons in key specialties, as well as anesthesiologists. Pacira will continue to act as the overall EXPAREL account manager.

Additional EXPAREL patent to issue that will extend protection until December 2021. The company has received an issue notification from the United States Patent and Trademark Office (USPTO) regarding its patent application 11/678,615, which is entitled "Production of Multivesicular Liposomes." The USPTO projects that the application will issue with the patent number 9,585,838 on March 7, 2017. The patent includes a patent term adjustment and will expire on December 24, 2021. Once listed, this will be the company’s third patent listed in the Orange Book for EXPAREL.
Fourth Quarter 2016 Financial Results

EXPAREL net product sales were $71.4 million in the fourth quarter of 2016, a 6% increase over the $67.2 million reported for the fourth quarter of 2015.

Total revenues were $72.9 million in the fourth quarter of 2016, a 5% increase over the $69.3 million reported for the fourth quarter of 2015.

Total operating expenses were $75.4 million in the fourth quarter of 2016, compared to $70.1 million in the fourth quarter of 2015.

GAAP net loss was $4.0 million, or $0.11 per share (basic and diluted), in the fourth quarter of 2016, compared to a GAAP net loss of $2.5 million, or $0.07 per share (basic and diluted), in the fourth quarter of 2015.

Non-GAAP net income was $3.6 million, or $0.10 per share (basic) and $0.09 per share (diluted), in the fourth quarter of 2016, compared to non-GAAP net income of $8.3 million, or $0.22 per share (basic) and $0.20 per share (diluted), in the fourth quarter of 2015.

Pacira had 37.4 million basic weighted average shares of common stock outstanding in the fourth quarter of 2016.

For non-GAAP measures, Pacira had 39.7 million diluted weighted average shares of common stock outstanding in the fourth quarter of 2016.
Full-Year 2016 Financial Results

EXPAREL net product sales were $265.8 million in 2016, an 11% increase over the $239.9 million in 2015.

Total revenues were $276.4 million in 2016, an 11% increase over the $249.0 million in 2015.

Total operating expenses were $308.4 million in 2016, compared to $239.5 million in 2015.

GAAP net loss was $37.9 million, or $1.02 per share (basic and diluted), in 2016, compared to GAAP net income of $1.9 million, or $0.05 per share (basic) and $0.04 (diluted), in 2015.

Non-GAAP net income was $25.2 million, or $0.68 per share (basic) and $0.62 per share (diluted), in 2016, compared to non-GAAP net income of $39.4 million, or $1.08 per share (basic) and $0.95 per share (diluted), in 2015.

Pacira ended 2016 with cash, cash equivalents and short-term investments ("cash") of $172.6 million.

Pacira had 37.2 million basic weighted average shares of common stock outstanding in 2016.

For non-GAAP measures, Pacira had 40.5 million diluted weighted average shares of common stock outstanding in 2016.
2017 Outlook

Pacira announces its full year 2017 financial guidance as follows. Pacira expects:

EXPAREL net product sales of $290 million to $310 million.

Non-GAAP gross margins of approximately 70%.

Non-GAAP research and development (R&D) expense of $50 million to $60 million.

Non-GAAP selling, general and administrative (SG&A) expense of $145 million to $155 million.

Stock-based compensation of $30 million to $35 million.
See "Non-GAAP Financial Information" and "Reconciliations of GAAP to Non-GAAP 2017 Financial Guidance" below.

FDA Accepts New Drug Application and Grants Priority Review for Enasidenib in Relapsed or Refractory AML with an IDH2 Mutation

On March 1, 2017 Celgene Corporation (CELG) and Agios Pharmaceuticals (AGIO) reported that the U.S. Food and Drug Administration (FDA) has accepted Celgene’s New Drug Application (NDA) for enasidenib (AG-221/CC-90007) for the treatment of patients with relapsed or refractory acute myeloid leukemia (AML) with an isocitrate dehydrogenase 2 (IDH2) mutation (Press release, Agios Pharmaceuticals, MAR 1, 2017, View Source;p=RssLanding&cat=news&id=2250587 [SID1234517906]). The NDA was granted Priority Review and has been given a Prescription Drug User Fee Act (PDUFA) action date of Aug. 30, 2017. Celgene completed the NDA submission in late December 2016.

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"We accelerated this application – submitting the NDA just three years after the first patient was treated in the enasidenib pivotal investigational trial – because we believe that there is a significant unmet need for people with relapsed or refractory AML," said Michael Pehl, president, Hematology/Oncology for Celgene. "The acceptance of the enasidenib NDA is a significant milestone in what we hope will be a new era of molecularly targeted therapies for patients with this devastating disease."

Enasidenib is a first-in-class, oral, targeted inhibitor of mutant IDH2. The NDA submission is based on results from AG221-C-001, a single-arm phase I/II study of enasidenib in patients with advanced hematologic malignancies with an IDH2 mutation. Early data from the relapsed or refractory AML patients in this study were presented at the 2015 American Society of Hematology (ASH) (Free ASH Whitepaper) Annual Meeting.

"Having received NDA acceptance and priority review for enasidenib, we look forward to working with our partner Celgene and the FDA to advance a first-in-class therapy for relapsed or refractory AML with an IDH2 mutation," said David Schenkein, M.D., chief executive officer at Agios. "We hope that the continued adoption of molecular profiling and availability of new targeted therapies such as enasidenib will have a significant impact on patients living with AML."

Additionally, Abbott has submitted a Premarket Approval (PMA) application for the FDA approval of an IDH2 assay on the Abbott m2000 RealTime System, a polymerase chain reaction (PCR) molecular diagnostics instrument. IDH2 mutations occur in about 8 to 19 percent of AML patients. Recent publications have highlighted the advances in the understanding of the genetics underlying AML and the need for routine mutational analysis at diagnosis and relapse.

Celgene is also evaluating enasidenib compared with conventional therapy in older patients with an IDH2 mutation and relapsed or refractory AML in the ongoing phase III IDHENTIFY trial (NCT02577406).

Enasidenib is an investigational drug that has not been approved for any use in any country.

About Acute Myelogenous Leukemia (AML)

AML, a cancer of blood and bone marrow characterized by rapid disease progression, is the most common acute leukemia affecting adults. Undifferentiated blast cells proliferate in the bone marrow rather than mature into normal blood cells. AML incidence significantly increases with age, and according to the American Cancer Society, the median age of onset is 66. Less than 10 percent of U.S. AML patients are eligible for bone marrow transplant and the vast majority of patients do not respond to chemotherapy and progress to relapsed/refractory AML. The five-year survival rate for AML is approximately 20 to 25 percent. IDH2 mutations are present in about 8 to 19 percent of AML cases.

Finding and Evaluating Oncology Opportunities at BIO Asia 2017 – A 1stOncology Insights Report

The BIO Asia 2017 meeting is an exclusive partnering forum offering an unique possibility to find and evaluate oncology opportunities in an Asian setting (1stOncology Insights, BioSeeker Group, MAR 1, 2017, http://www.bioseeker.com/market-research-report/finding-and-evaluating-oncology-opportunities-at-bio-asia-2017-a-1stoncology-insights-report.html [SID1234518080]).
In a recent analysis, based on the communicated participants at the time*, the oncology position and activities of 61 companies has been featured by the analyst team at 1stOncology for the benefit its audience. In overall, an extensive partnering review has been done of close to 900, partnered or as yet un-partnered, drugs in 17 "hot" areas in oncology, including:

· Most recent Positive/Negative Developments (226/43)
· Start-Ups (4)
· Fierce 15 Drugs (53)
· Orphan Drugs (252)
· Breakthrough Therapies (31)
· Cancer Vaccines (59)
· CAR/TCR Therapies (14)
· Immune Checkpoints (67)
· Epigenetic Therapies (35)
· Protein Kinase Inhibitors (194)
· Antibodies in Oncology (345)
· Cancer Peptides (47)
· RNA Therapies (13)
· Conjugated Drugs (109)
· Biomarker/Companion Diagnostic Drugs (166)
· Combination Therapy Drugs (492)
· Biosimilars/Biobetters (27)

Area (Number of Drugs in Each Area)

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This independent, third-party breakdown analysis gives a landscape of oncology opportunities which guides corporate interest in how to allocate time and spend resources around BIO Asia where it reaps the most value. Undoubtedly, immuno-oncology will continue being the center piece of attention in general and immunecheck point inhibitors in particular.

Furthermore almost one thousand corporate developments have been analyzed detailing the latest positive and negative pipeline development for circa 250 top cancer drugs throughout 2016 to present, giving a comprehensive insight to current developments such as successful clinical trials, trials with missed primary endpoints, new or terminated partnerships, M&A and much more.

The 1stOncology team recognizes that contacts are key to actively drive forward partnering activities so special for BIO Asia 2017 they have set out to boost the event with giving access to circa 300 contacts in business development and licensing people within the featured companies, allowing the thrifty to reach out quickly and directly to the right person of interest for initial introductions, partnership discussions, pre-booking meetings etc.

*As of February 24, 2017