Transgene and BioInvent – First patient treated in Part B of Phase I trial assessing the novel oncolytic virus BT-001 in combination with KEYTRUDA® (pembrolizumab)

On October 10, 2023 Transgene (Euronext Paris: TNG), a biotech company that designs and develops virus-based immunotherapeutics against cancer, and BioInvent International AB ("BioInvent") (Nasdaq Stockholm: BINV), a biotech company focused on the discovery and development of novel and first-in-class immune-modulatory antibodies for cancer immunotherapy, reported that the first patient of the Phase I part B clinical trial evaluating the combination of BT-001 and MSD’s anti-PD-1 therapy, KEYTRUDA (pembrolizumab) has been dosed (Press release, Transgene, OCT 10, 2023, View Source [SID1234635723]).

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The Phase I Part B of the trial explores repeated intra-tumoral injections of BT-001 in combination with intravenous infusions of KEYTRUDA. Transgene and BioInvent plan to enroll a minimum of 12 patients with metastatic or advanced solid tumors, including melanoma. In accordance with our clinical trial and supply agreement, KEYTRUDA is being supplied by MSD (a tradename of Merck & Co., Inc., Rahway, NJ, USA). Trial endpoints include safety, evaluation of efficacy, and assessment of immune changes in the tumor microenvironment.

Transgene and BioInvent are co-developing BT-001, an oncolytic virus designed using Transgene’s Invir.IO platform encoding BioInvent’s differentiated anti-CTLA-4 antibody and human GM-CSF cytokine to elicit a strong and effective anti-tumoral response. The drug is currently being evaluated against solid tumors in a Phase I/IIa clinical trial as a single agent and in combination with the PD-1 checkpoint inhibitor KEYTRUDA.

The inclusion of the last patient in Part B of the study is expected in H1 2024.

Previously reported Phase I data confirmed the mechanism of action of BT-001 as a single agent and demonstrated first signs of anti-tumoral activity.

Dr. Martin Welschof, CEO of BioInvent and Dr. Alessandro Riva, Chairman and CEO of Transgene, added: "By combining BT-001 with pembrolizumab, we are building upon the promising data generated by BT-001 as a single agent. Targeting the PD1/PD-L1 pathway in addition to BT-001’s mechanism of action is expected to further stimulate and restore the patient’s immune system, which should result in improved antitumoral activity and patient outcome. We are thrilled to enter this new phase of the development of the novel oncolytic virus BT-001 and further demonstrate its potential in combination with a reference treatment."

KEYTRUDA is a registered trademark of Merck Sharp & Dohme LLC, a subsidiary of Merck & Co., Inc., Rahway, NJ, USA.

About the trial

The ongoing Phase I/IIa (NCT: 04725331) study is a multicenter, open label, dose-escalation trial evaluating BT-001 as a single agent and in combination with pembrolizumab (anti-PD-1 treatment). Patient inclusions are ongoing in Europe (France, Belgium) and the trial has been authorized in the US.

This Phase I is divided into two parts. In part A, patients with metastatic/advanced tumors received single agent, intra-tumoral administrations of BT-001. Part B is exploring intra-tumoral injections of BT-001 in combination with KEYTRUDA. In this part, KEYTRUDA is being provided to the trial by MSD (a tradename of Merck & Co., Inc., Rahway, NJ, USA).

The Phase IIa will evaluate the combination regimen in several patient cohorts with selected tumor types. These expansion cohorts will offer the possibility of exploring the activity of this approach to treat other malignancies not traditionally addressed with this type of treatment.

About BT-001

BT-001 is an oncolytic virus generated using Transgene’s Invir.IO platform and its patented large-capacity VVcopTK-RR- oncolytic virus, which has been engineered to encode both a Treg-depleting recombinant human anti-CTLA-4 antibody generated by BioInvent’s proprietary n-CoDeR/F.I.R.S.T platforms, and the human GM-CSF cytokine. By selectively targeting the tumor microenvironment, BT-001 is expected to elicit a much stronger and more effective antitumoral response. Therefore, by reducing systemic exposure, the safety and tolerability profile of the anti-CTLA-4 antibody may be greatly improved.

BT-001 is being co-developed as part of a 50/50 collaboration on oncolytic viruses between Transgene and BioInvent. To know more on BT-001, watch our video here.

HiFiBiO Therapeutics Receives Approval from Chinese NMPA for IND Application for HFB200301, an Innovative Anti-Tumor Monoclonal Antibody

On October 9, 2023 HiFiBiO Therapeutics, a clinical stage global biotech company focusing on improving patient lives with single cell precision, reported that the Chinese National Medical Products Administration (NMPA) has approved the company’s Investigational New Drug (IND) application for HFB200301, a pioneering, first-in-class anti-TNFR2 agonistic monoclonal antibody (Press release, HiFiBiO Therapeutics, OCT 10, 2023, View Source [SID1234635720]).

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HFB200301 is currently undergoing Phase I clinical trial (NCT05238883) evaluation in the treatment of advanced solid tumors in the United States and Europe, both as a monotherapy and in combination with tislelizumab, an anti-PD-1 immune checkpoint inhibitor. This trial is guided by HiFiBiO’s proprietary Drug Intelligence Science (DIS) platform, which utilizes patient data to optimize dosages, dosing regimens, indication selection, and biomarker strategies.

Liang Schweizer, PhD, Founder, Chairperson, and CEO of HiFiBiO Therapeutics, commented on this significant development, saying, "The approval of our HFB200301 IND by the NMPA represents yet another pivotal milestone for the program, confirming our strong commitment to developing safe and effective treatments for cancer patients globally."

"Incorporating Chinese patients into our study will provide invaluable insights into the therapeutic potential of HFB200301 across a diverse patient population, ultimately guiding our efforts to develop novel immuno-oncology treatments to patients with significant unmet medical needs," emphasized Robert Andtbacka, MD, CM, CMO of HiFiBiO Therapeutics.

Under the terms of the previously announced clinical supply agreement, Novartis will supply tislelizumab for use in combination with HFB200301, and HiFiBiO Therapeutics will maintain control of the HFB200301 program, including global R&D and commercial rights.

HFB200301

HFB200301 is a first-in-class anti-TNFR2 agonistic monoclonal antibody that binds potently and selectively to TNFR2, and induces the activation of CD4 T cells, CD8 T cells, and NK cells. HFB200301 demonstrates potent antitumor activity as a monotherapy and in combination with anti-PD-1 in animal tumor models. HiFiBiO is implementing a biomarker strategy, leveraging its DIS platform, to identify indications that may benefit the most from HFB200301 as a monotherapy or as a combination therapy.

Tislelizumab
Tislelizumab, an investigational humanized IgG4 anti-PD-1 monoclonal antibody, is designed to minimize binding to Fc-gamma (Fcγ) receptors on macrophages. Pre-clinical studies have shown that binding to Fcγ receptors on macrophages can compromise the anti-tumor activity of PD-1 antibodies through activation of antibody-dependent macrophage-mediated killing of T effector cells.

Development of small molecule inhibitors targeting RNA helicase DHX33 as anti-cancer agents Article published in BMCL

On October 9, 2023 Kaiyue Life reported the company and other institutions jointly published a paper titled "Development of small molecule inhibitors targeting RNA helicase DHX33 as anti-cancer agents" in the classic journal of medicinal chemistry, Bioorganic and Medicinal Chemistry Letters (BMCL) (Press release, KeYe Life Technologies, OCT 9, 2023, View Source;article_id=84 [SID1234644610]).

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Recently, a collaborative paper titled "Development of small molecule inhibitors targeting RNA helicase DHX33 as anti-cancer agents" co-authored by Kaiyue Life Sciences, the University of Macau, Southern University of Science and Technology, and Heya Pharmaceuticals was published online in BMCL, a long-established journal of medicinal chemistry.

The RNA helicase DHX33 has been identified as a key player in promoting cancer development. Genetic deletion of DHX33 significantly blocks tumorigenesis. Importantly, its helicase activity was found to be critical for exerting cellular functions. In this study, a helicase-based high-throughput screening (HTS) technique was used to discover DHX33 inhibitors from the Chembridge chemical library containing 15,000 small molecules. We discovered a lead compound containing a benzimidazole ring that showed some selectivity for DHX33. Further structural optimization led to the design and synthesis of a series of mimetic inhibitors. Considering the potential role of DHX33 in cancer development, we evaluated these compounds based on their cytotoxic activity against U251-MG cancer cells in vitro. Among them, compound IVa (KY386) was identified as a selective inhibitor of DHX33 helicase with strong anticancer activity and moderate metabolic stability. These results support the important role of DHX33 inhibitors in the development of novel anticancer drugs.

InCephalo receives a Eurostars grant

On October 9, 2023 InCephalo AG reported the company , University of Basel and VitroScan receive a competitive Eurostars grant (€2.3M) to accelerate the development of promising new drugs for Glioblastoma patients – CLEIO (Press release, InCephalo Therapeutics, OCT 9, 2023, View Source [SID1234644133]).

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The consortium led by InCephalo AG has received the competitive Eurostar grant. The Swiss – Dutch consortium consist of three collaborating partners: InCephalo AG, University of Basel and VitroScan.
In the CLEIO project: The first-in-kind Compartment Locked and Effective ImmunOtherapy against glioblastoma, the consortium will: i) study the effect of InC01 (InCephalo’s primary asset) treatment on established ex- vivo GBM models based on patient tissue, ii) discover new biomarkers for the response and non-response of InC01, and iii) drive clinical Phase II trial design through stratification of patient populations.

«We are excited to receive this grant as will allow us to de-risk our
clinical development at such an early stage» says Dr. Carlo Bertozzi,
CEO and co-founder of InCephalo.

Willemijn Vader, CEO VitroScan:

«It is a great opportunity for VitroScan to collaborate with these partners and integrate our expertise to develop predictive tools for new novel treatment options for glioblastoma patients».

Prof. G. Hutter, Neurosurgeon and Group leader at both the Unversity of Basel and the University Hospital in Basel:

«As a treating physician, I see that novel therapeutic modalities are needed for brain cancer patients. In this collaboration, we are actively working to push InC01, a promising new modality, closer to the patient and on the way learn more about which patients are more likely to react».

Coeptis Therapeutics to Participate in Panel at the BioFlorida Conference Discussing Emerging Cell and Gene Therapies

On October 9, 2023 Coeptis Therapeutics Holdings, Inc. (NASDAQ: COEP) ("Coeptis" or "the Company"), a biopharmaceutical company developing innovative cell therapy platforms for cancer, reported that Dan Yerace, Director and Vice President of Operations, will participate in a panel titled, "Ambitious Innovation: Emerging Cell and Gene Therapies," at the BioFlorida Conference on Thursday October 12th from 11:50 AM-12:50 PM (Press release, Coeptis Therapeutics, OCT 9, 2023, View Source [SID1234635732]).

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Details of the panel discussion are as follows:

Event:

BioFlorida Conference

Date & Time:

October 12, 2023, at 11:50 AM, EDT

Panel Title

Ambitious Innovation: Emerging Cell and Gene Therapies

Location:

Sawgrass Marriott Golf Resort & Spa, Ponte Vedra Beach, FL