AN2 Therapeutics Presents Clinical and Translational Data Supporting Development of Epetraborole for Polycythemia Vera at the Society of Hematologic Oncology (SOHO) 2026 Annual Meeting

On August 31, 2026 AN2 Therapeutics, Inc. (Nasdaq: ANTX), a clinical stage biopharmaceutical company focused on the discovery and development of novel small molecule therapeutics derived from its boron chemistry platform, reported that four abstracts highlighting clinical and nonclinical data supporting the development of epetraborole, a novel boron-containing oral candidate for the treatment of polycythemia vera (PV), will be presented at the Society of Hematologic Oncology (SOHO) 2026 Annual Meeting, taking place September 9-12, 2026, at the George R. Brown Convention Center in Houston, Texas.

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"These abstracts provide insights into the potential beneficial hematological effects of epetraborole across both clinical and nonclinical studies and strengthen our understanding of the exposure-response relationships that we believe support its development in polycythemia vera," said George H. Talbot, M.D. Co-Founder and Senior Medical Advisor of AN2 Therapeutics.

Key Highlights:

Clinical and nonclinical studies demonstrated potential beneficial effects of epetraborole on erythropoiesis and hemoglobin-related parameters.
Data further characterized the hematological and safety profile of epetraborole across healthy volunteers, non-PV patients, and nonhuman primate models.
Exposure-response relationships observed in nonhuman primates were predictive of effects subsequently observed in humans, supporting the translational relevance of these models.
Collectively, the findings support the ongoing clinical development of epetraborole as a potential oral treatment for PV.
SOHO 2026 Abstracts:

Poster Number

Title

MPN-1041

Epetraborole Demonstrates an Exposure-Dependent Effect on Erythropoiesis in Healthy Subjects

MPN-1076

Hematological and Safety Profile of Epetraborole in a Non-Polycythemia Vera Patient Population

MPN-1082

Exposure-Response Analyses of Hemoglobin Changes During Epetraborole Administration to Nonhuman Primates Predict Human Exposure-Response Relationships

MPN-1106

Hematological Profile in Nonhuman Primates of Epetraborole, a Novel Boron-Containing Candidate for Oral Treatment of Polycythemia Vera

Copies of the abstracts will be available on the Presentations and Publications section of the AN2 Therapeutics website at the following link: View Source

(Press release, AN2 Therapeutics, AUG 31, 2026, View Source [SID1234670466])

Astellas enters voluntary agreement with U.S. government supporting affordable access to medicines

On August 31, 2026 Astellas Pharma Inc. (TSE: 4503, President and CEO: Naoki Okamura, "Astellas") reported that it has reached an agreement with the U.S. government that reflects our commitment to patient access, affordability and innovation, while reinforcing Astellas’ longstanding commitment to the U.S. healthcare system.

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Under the agreement, Astellas will take the following actions:

Lower the prices of medicines in Medicaid and establish pricing for future medicines aligned with other developed nations that reflect international market conditions, innovation, and patient value.
Further the resilience of the supply chain for important medicines by donating 25 kg of tacrolimus active pharmaceutical ingredient (API), the standard used to prevent solid organ transplant rejection, to the U.S. Strategic Active Pharmaceutical Ingredients Reserve (SAPIR).
Additional terms of the agreement are not being disclosed.

This agreement reflects our longstanding commitment to improving access for patients while continuing to invest in the research and development of innovative medicines. We believe patients benefit most when affordability and innovation advance together, and we remain committed to working collaboratively with governments and healthcare stakeholders around the world to achieve both objectives for patients with serious unmet medical needs.

With U.S. headquarters in Northbrook, Ill., Astellas has a significant research, manufacturing, and economic footprint in the U.S. that supports patients, jobs and communities spanning from Massachusetts to California. Within the past ten years, Astellas has opened two new cutting-edge manufacturing facilities in the U.S., including a cell therapy manufacturing facility in Westborough, Mass., and a gene therapy manufacturing facility in Sanford, North Carolina. In 2024, Astellas also opened two new research centers – our West Coast Innovation Center in South San Francisco and the Astellas Life Sciences Center in Cambridge, Mass.

(Press release, Astellas, AUG 31, 2026, View Source [SID1234670464])

T-MAXIMUM B7-H3-Targeted Allogeneic CAR-T Therapy MT027 Receives FDA Fast Track Designation, Accelerating Global Development for Intracranial Solid Tumors

On August 31, 2026 T-MAXIMUM PHARMACEUTICAL Inc. ("T-MAXIMUM") reported that its investigational allogeneic CAR-T cell therapy MT027 has been granted Fast Track Designation (FTD) by the U.S. Food and Drug Administration (FDA) for the treatment of recurrent glioblastoma.

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MT027 had previously received FDA Orphan Drug Designation (ODD) for the treatment of recurrent high-grade glioma, and clearance from the FDA to conduct a Phase II clinical study in recurrent glioblastoma. Together, the Orphan Drug Designation, the Phase II clearance and the newly granted Fast Track Designation add further momentum to the global development of MT027.

A Competitive B7-H3 Field: Allogeneic CAR-T Charts a Differentiated Course

B7-H3 has emerged in recent years as a target of significant interest in solid tumor drug development, with antibody-drug conjugates (ADCs), antibody therapeutics and cell therapies all being actively pursued. In July 2026, Hansoh Pharmaceutical announced that its B7-H3 ADC, HS-20093, met the primary endpoint of progression-free survival (PFS) as assessed by an independent review committee (IRC) in patients with relapsed or progressive osteosarcoma in the pivotal Phase III ARTEMIS-011 study. Developments across the field indicate that the clinical value of B7-H3 continues to be validated along multiple technology routes.

Against this backdrop, MT027 is differentiated by the combination of three elements: B7-H3 targeting, an allogeneic "off-the-shelf" product format, and a locoregional intracavitary route of administration — directed at recurrent glioblastoma and brain metastases, settings of high unmet medical need.

From a Single Asset to a Method: Building a Verifiable, Repeatable Translational Approach for Intracranial Solid Tumors

For T-MAXIMUM, the significance of MT027 extends beyond the advancement of one pipeline asset. Recurrent glioblastoma is among the most demanding settings in which to test the capabilities of cell therapy in solid tumors. It requires solving the delivery of cells to compartments associated with the central nervous system, while at the same time addressing the in vivo persistence of allogeneic cells, safety monitoring following local administration, and the clinical execution of repeat dosing and long-term follow-up.

What MT027 is exploring is a development methodology built around intracranial solid tumors — B7-H3 as the target, allogeneic universal CAR-T as the product format, and local intracavitary delivery as the route of administration — refined through clinical research across patient selection, dosing, monitoring and the accumulation of evidence.

If this approach continues to generate high-quality evidence in recurrent glioblastoma, its value may not be limited to a single indication. The company is also exploring the potential of MT027 in brain metastases and in other solid tumor settings suited to local delivery. Based on the company’s prior disclosure, preliminary first-in-human data in brain metastases are planned for formal presentation during the World Conference on Lung Cancer (WCLC) in September 2026.

Fast Track Designation: Added Speed for Global Development

Fast Track is an FDA process designed to facilitate the development of drugs that treat serious conditions and address unmet medical needs. A sponsor whose program receives the designation has the opportunity for more frequent interactions with the FDA over the course of drug development, and, where the relevant criteria are met, the program may also be eligible for Rolling Review of a marketing application, as well as for Accelerated Approval and Priority Review. These mechanisms are intended to support a more efficient path for the clinical development and potential registration of MT027 in the United States and, if development is successful, earlier treatment access for patients with recurrent glioblastoma worldwide.

MT027’s existing Orphan Drug Designation confers benefits including FDA guidance on clinical development, tax credits for qualified clinical trials, exemption from certain application fees, and seven years of market exclusivity in the designated indication upon approval. With the addition of Fast Track Designation, MT027 now holds dual designations under the FDA regulatory framework, further consolidating its position as one of the leading global allogeneic CAR-T programs in solid tumors.

Company Comment

"Receiving Fast Track Designation from the FDA is an important milestone in the global development of MT027, but it is not the destination," said Xiaoyun Shang, CEO of T-MAXIMUM PHARMACEUTICAL. "What matters more to us is the continued validation — in the demanding setting of recurrent glioblastoma — of how target selection, an allogeneic off-the-shelf product, local delivery and clinical execution work together. Every piece of solid clinical evidence helps us refine the ongoing development of MT027 and provides translational experience that can inform our next-generation products and other intracranial solid tumor settings suited to local delivery. Going forward, T-MAXIMUM will continue to be guided by patient needs, and to advance allogeneic CAR-T in solid tumors on a foundation of safety, rigor and verifiable evidence."

(Press release, T-MAXIMUM Pharmaceutical, AUG 31, 2026, View Source [SID1234670463])

IDEAYA Biosciences Announces Successful FDA Type C Meeting for IDE849, DLL3 TOP1 ADC, on Phase 3 Registrational Trial Design for Potential Accelerated and Full Approval in Extensive Stage Small Cell Lung Cancer

On August 31, 2026 IDEAYA Biosciences, Inc. (NASDAQ: IDYA), a precision medicine oncology company committed to the discovery and development of targeted therapeutics, reported a successful FDA Type C meeting to determine the Phase 3 registrational trial design for IDE849, a potential best-in-class delta-like ligand 3 (DLL3)-targeting Topo-I-payload antibody drug conjugate (ADC), in extensive stage small cell lung cancer (ES-SCLC). IDEAYA is targeting to initiate the Phase 3 registrational study in ES-SCLC by year-end 2026.

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"Based on the FDA Type C meeting, we are targeting to initiate a randomized Phase 3 registrational study for IDE849 monotherapy in extensive stage small cell lung cancer to enable a potential accelerated approval and full approval in one seamless study design," said Yujiro S. Hata, President and Chief Executive Officer, IDEAYA Biosciences. "We also look forward to the clinical data updates at ESMO (Free ESMO Whitepaper) 2026 and later this year from our company sponsored clinical trial in ES-SCLC and NEC to support a potential best-in-class profile."

The anticipated enrollment target for the IDEAYA-sponsored global Phase 3 registrational study is approximately 400 ES-SCLC patients with prior tarlatamab treatment. The study will be randomized 1:1 between the treatment and an investigator’s choice control arm that will include topotecan and ambrucin. The primary endpoint for accelerated approval will be overall response rate (ORR) by blinded independent central review (BICR) and the primary endpoint for full approval will be median overall survival. The secondary endpoints will include median duration of response by BICR, progression free survival, safety, among others.

IDEAYA has an ongoing multi-site global Phase 1 clinical trial for IDE849 in DLL3 upregulated solid tumor indications, including SCLC, and neuroendocrine carcinomas (NEC) (NCT07174583). The study is enrolling patients globally, including in North America, Europe, Australia, South America, and Asia. In this ongoing Phase 1 dose escalation study, IDE849 is currently evaluating the expansion doses of 2.4 mg/kg and 3.5 mg/kg IV once every 3-weeks (Q3W) to determine the recommended Phase 3 dose (RP3D).

In addition, IDE849 is being evaluated in clinical combination study with AstraZeneca’s PDL1 inhibitor Imfinzi, and IDEAYA’s potential first-in-class Phase 1 PARG inhibitor, IDE161, to determine a potential first-line (1L) SCLC Phase 3 registrational trial design. IDE161 prevents the removal of poly(ADP-ribose) chains generated by PARP during the DNA damage response, leading to persistent PARylation and impaired resolution of DNA repair complexes. Together with TOP1-payload ADCs, this unique mechanism-of-action results in sustained TOP1 cleavage complexes and the accumulation of DNA damage that delivers enhanced anti-tumor activity. We believe this potential first-in-class combination has the potential to enhance durability of IDEAYA’s TOP1-payload based ADC pipeline, including IDE849 and IDE034 (Phase 1 B7H3/PTK7 Bispecific TOP1 ADC).

DLL3 has been reported to be upregulated in multiple solid tumor types, including in SCLC, NEC and melanoma, among others. IDEAYA estimates the annual incidence of SCLC and NEC in the United States is approximately 34,000 and 19,000 patients, respectively. DLL3 has limited extracellular expression in normal tissues, making it a promising potential therapeutic target in these solid tumors, for which there remains significant unmet medical need.

(Press release, Ideaya Biosciences, AUG 31, 2026, View Source [SID1234670462])

TransCode Therapeutics Announces Publication Demonstrating Survival Benefit of TTX-MC138 in Preclinical Model of Breast Cancer Bone Metastasis

On August 31, 2026 TransCode Therapeutics, Inc. (NASDAQ: RNAZ), a clinical stage company pioneering immuno-oncology and RNA-based therapeutics for the treatment of high risk and advanced cancers, reported the publication of a peer-reviewed article in Cancers titled, "Targeting miR-10b in Breast Cancer Bone Colonization Model Using Image-Guided Nucleic Acid-Based Therapeutics." The study reports that TransCode’s lead therapeutic candidate, TTX-MC138, produced significant survival benefits in a preclinical model of breast cancer bone metastasis while demonstrating favorable tolerability and no observed systemic toxicity.

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The publication builds on a growing body of evidence supporting microRNA-10b (miR-10b) as an important driver of cancer metastasis and further validates TransCode’s therapeutic approach of inhibiting miR-10b using proprietary oligonucleotide nanotechnology.

The study was led by Dr. Anna Moore, Professor in the Radiology and Physiology Departments, Director of the Precision Health Program and Associate Dean for Research Development at the College of Human Medicine at Michigan State University. Dr. Moore is a co-founder of TransCode Therapeutics and Chair of the Scientific Advisory Board, and a globally recognized expert in molecular imaging and RNA-targeted cancer therapeutics.

"Metastatic disease remains responsible for the overwhelming majority of cancer deaths, and effective therapies specifically designed to target metastasis remain limited," said Zdravka Medarova, Ph.D., Chief Scientific Officer of TransCode Therapeutics and co-author of the publication. "These findings demonstrate that miR-10b inhibition can significantly impact survival in a challenging model of metastatic cancer and further support the potential applicability of our platform across multiple metastatic tumor types."

Key Findings

Among the study’s findings:

TTX-MC138 successfully accumulated in metastatic bone lesions in a mouse model of bone cancer bone metastasis following systemic administration.
Treatment significantly reduced expression of miR-10b, a microRNA implicated in metastatic progression, and increased expression of HOXD10, a downstream tumor-suppressor target.
Animals treated with anti-miR-10b therapeutics demonstrated significant survival benefits compared with controls.
Repeated dosing was well tolerated, with no evidence of systemic toxicity observed during the study.
The results support the use of image-guided anti-miR-10b nanotherapeutics as a potentially translatable strategy for treating metastatic cancer.
Bone is the most common site of metastatic spread in breast cancer and represents a major unmet medical need, with patients experiencing substantial morbidity and poor long-term outcomes. The authors concluded that targeting miR-10b using an image-guided anti-miR-10b nanotherapeutic represents a promising and translatable strategy for treating breast cancer bone metastases.

Relevance to TransCode’s Clinical Program

While TransCode’s current clinical development efforts are focused on metastatic cancers and its ongoing TTX-MC138 program in molecular residual disease-positive colorectal cancer, the newly published findings suggest potential future applicability of miR-10b inhibition across additional metastatic disease settings where tumor spread drives poor outcomes.

The article was published online on August 23, 2026, in Cancers, a peer-reviewed oncology journal.

About TTX-MC138

TTX-MC138 is a first-in-class therapeutic candidate designed to inhibit microRNA-10b, or miR-10b, a microRNA widely believed to be critical to the emergence and progression of many metastatic cancers. TransCode’s Phase 1a first-in-human clinical trial achieved its primary safety endpoint and established a recommended Phase 2 dose, as announced at ESMO (Free ESMO Whitepaper) 2025.

(Press release, TransCode Therapeutics, AUG 31, 2026, View Source [SID1234670461])