argenx Reports Third Quarter 2023 Financial Results and Provides Business Update

On October 31, 2023 argenx SE (Euronext & Nasdaq: ARGX), a global immunology company committed to improving the lives of people suffering from severe autoimmune diseases, reported its third quarter 2023 financial results and provided a business update and outlook for the remainder of the year (Press release, argenx, OCT 31, 2023, View Source,the%20same%20periods%20in%202022. [SID1234636455]).

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"We continue to prioritize patient impact with VYVGART and VYVGART Hytrulo, broadening our two gMG products into earlier treatment lines and new geographies. VYVGART has now been used in thousands of patients over multiple treatment years, and its unique clinical profile has built patient trust and physician confidence in the brand," said Tim Van Hauwermeiren, Chief Executive Officer of argenx. "There is a significant opportunity before us to transform autoimmunity across multiple indications with VYVGART. Based on the successful ADHERE trial, we are ready to file the sBLA by the end of 2023 to bring our first-in-class FcRn blocker to CIDP patients as quickly as possible. We are also on track with two near-term pivotal readouts and an ambitious plan forward over the coming years as we continue to execute and drive innovation within our FcRn portfolio and across immunology more broadly."

THIRD QUARTER 2023 AND RECENT BUSINESS UPDATE

VYVGART Expansion

VYVGART is a first-in-class antibody fragment targeting the neonatal Fc receptor (FcRn) and is now approved globally in seven countries or regions (U.S., Japan, EU, UK, Israel, China, Canada) for generalized myasthenia gravis (gMG). VYVGART Hytrulo (subcutaneous (SC) injection) was approved in the U.S. in June 2023. argenx is planning for multi-dimensional expansion to reach more patients with gMG and other severe autoimmune diseases through additional global regulatory approvals.

Generated global net product revenues (inclusive of both VYVGART and VYVGART Hytrulo) of $329 million in the third quarter of 2023
Health Canada approved VYVGART on September 21, 2023, marking the seventh global approval for gMG
European Commission (EC) approval of SC efgartigimod for gMG expected in fourth quarter of 2023 following positive recommendation from Committee for Medicinal Products for Human Use (CHMP) of the European Medicines Agency (EMA)
Japan approval decision regarding SC efgartigimod for gMG expected by first quarter of 2024
Japan marketing authorization application (MAA) filed for VYVGART for primary immune thrombocytopenia (ITP); approval decision expected in first quarter of 2024
U.S. supplemental Biologics License Application (sBLA) for VYVGART Hytrulo in chronic inflammatory demyelinating polyneuropathy (CIDP) on track to be filed by end of 2023
China approval decision regarding SC efgartigimod for gMG expected by end of 2024 through partnership with Zai Lab

Efgartigimod Research and Development

argenx is solidifying its leadership in FcRn blockade and demonstrating the broad potential of efgartigimod by advancing its clinical development programs of IgG-mediated autoimmune diseases. By 2025, efgartigimod is expected to be approved, in regulatory review or in development in 15 severe autoimmune diseases

Topline data from ADVANCE-SC (ITP) expected in fourth quarter of 2023; results from ADVANCE-IV study were published in The Lancet in September 2023
Topline data from ADDRESS (pemphigus) and GO/NO GO decision from BALLAD (bullous pemphigoid) both expected around year-end 2023
GO/NO GO decision expected from ALKIVIA (myositis) in second half of 2024
Topline data from ALPHA (post-COVID postural orthostatic tachycardia syndrome (PC-POTS)) expected in first quarter of 2024 and RHO (Sjogren’s syndrome) in first half of 2024
Pipeline Progress

argenx is advancing a robust portfolio of innovative clinical programs, including empasiprubart (C2 inhibitor) and ARGX-119 (muscle-specific kinase (MuSK) agonist). Both programs have the potential to be first-in-class opportunities for multiple severe indications.

Topline data from Phase 2 ARDA study of empasiprubart (ARGX-117) in multifocal motor neuropathy (MMN) expected in 2024
Phase 1 study of ARGX-119 ongoing in healthy volunteers; subsequent Phase 1b trial planned to assess early signal detection in patients with congenital myasthenic syndrome (CMS) and amyotrophic lateral sclerosis (ALS)
Immunology Innovation Program

argenx continues to invest in its discovery engine, the Immunology Innovation Program, to foster a robust innovation ecosystem and drive early-stage pipeline growth. argenx expects to nominate one new pipeline candidate in 2023.

THIRD QUARTER 2023 FINANCIAL RESULTS

argenx SE

UNAUDITED CONDENSED CONSOLIDATED INTERIM STATEMENTS OF PROFIT OR LOSS

Three Months Ended
September 30, Nine Months Ended
September 30,
(in thousands of $ except for shares and EPS) 2023 2022 2023 2022
Product net sales $ 329,097 $ 131,329 $ 816,432 $ 227,325
Collaboration revenue 692 6,652 3,047 9,262
Other operating income 10,050 8,508 31,275 26,565
Total operating income $ 339,839 $ 146,489 $ 850,754 $ 263,152

Cost of sales $ (35,999) $ (10,264) $ (78,358) $ (16,646)
Research and development expenses (191,755) (236,681) (553,119) (515,568)
Selling, general and administrative expenses (191,930) (108,181) (503,079) (336,845)
Loss from investment in joint venture (743) - (2,623) -
Total operating expenses (420,427) (355,126) (1,137,179) (869,059)

Operating loss $ (80,588) $ (208,637) $ (286,425) $ (605,907)

Financial income $ 30,049 $ 8,007 $ 67,078 $ 13,740
Financial expense (231) (785) (626) (2,916)
Exchange gains/(losses) (32,509) (39,609) (23,345) (92,991)

Loss for the period before taxes $ (83,279) $ (241,024) $ (243,318) $ (688,074)
Income tax (expense)/benefit $ 10,637 $ 5,982 $ 47,437 $ 17,096
Loss for the period $ (72,642) $ (235,042) $ (195,881) $ (670,978)
Loss for the year attributable to: -
Owners of the parent $ (72,642) $ (235,042) $ (195,881) $ (670,978)
Weighted average number of shares outstanding 58,128,233 55,203,655 56,512,254 54,049,119
Basis and diluted loss per share (in $) (1.25) (4.26) (3.47) (12.41)
Net increase/(decrease) in cash, cash equivalents and current financial assets compared to year-end 2022 and 2021 $ 993,035 $ 48,813
Cash and cash equivalents and current financial assets at the end of the period $ 3,185,583 $ 2,385,541
DETAILS OF THE FINANCIAL RESULTS

Total operating income for the third quarter and year-to-date in 2023 was $339.8 million and $850.8 million, respectively, compared to $146.5 million and $263.2 million for the same periods in 2022, and mainly consists of:

Product net sales of VYVGART for the three months ended and nine months ended September 30, 2023, were $329.1 million and $816.4 million, compared to $131.3 million and $227.3 million for the same periods in 2022.
Other operating income for the third quarter and year-to-date in 2023 was $10.1 million and $31.3 million, respectively, compared to $8.5 million, and $26.6 million for the same periods in 2022. The other operating income for the three and nine months ended September 30, 2023, primarily relates to research and development tax incentives and payroll tax rebates. Other income also includes $0.7 million in royalty revenue from VYVGART sales in China.
Total operating expenses for the third quarter and year-to-date in 2023 were $420.4 million and $1,137.2 million, respectively, compared to $335.1 million and $869.1 million for the same periods in 2022, and mainly consists of:

Cost of sales for the third quarter and year-to-date in 2023 was $36.0 million and $78.4 million, respectively, compared to $10.3 million and $16.6 million for the same periods in 2022. The cost of sales was recognized with respect to the sale of VYVGART and VYVGART Hytrulo.
Research and development expenses for the third quarter and year-to-date in 2023 were $191.8 million and $553.1 million, respectively, compared to $236.7 million and $515.6 million for the same periods in 2022. The research and development expenses mainly relate to external research and development expenses and personnel expenses incurred in the clinical development of efgartigimod in various indications and the expansion of other clinical and preclinical pipeline candidates.
Selling, general and administrative expenses for the third quarter and year-to-date in 2023 were $191.9 million and $503.1 million, respectively, compared to $108.2 million and $336.8 million for the same periods in 2022. The selling, general and administrative expenses mainly relate to professional and marketing fees linked to the commercialization of VYVGART and VYVGART Hytrulo in the U.S., EU and Japan, and personnel expenses.

Financial income for the third quarter and year-to-date in 2023 was $30.0 million and $67.1 million, respectively, compared to $8.0 million and $13.7 million for the same periods in 2022. The increase in financial income is mainly due to an increase in interest income on current financial assets and cash and cash equivalents attributable to higher interest rates.

Exchange losses for the third quarter and year-to-date in 2023 were $32.5 million and $23.3 million respectively, compared to $39.6 million and $93.0 million of exchange losses for the same periods in 2022. Exchange gains/losses are mainly attributable to unrealized exchange rate gains or losses on the cash, cash equivalents and current financial assets position in Euro.

Income tax for the third quarter and year-to-date in 2023 was $10.6 million and $47.4 million of tax benefit, respectively, compared to $6.0 million and $17.1 million of tax benefit for the same periods in 2022. Tax benefit for the nine months ended September 30, 2023, consists of $23.8 million of income tax expense and $71.3 million of deferred tax income, compared to $15.0 million of income tax expense and $32.1 million of deferred tax income for the comparable prior period.

Net loss for the three and nine-month periods ended September 30, 2023, was $72.6 million and $195.9 million, respectively, compared to $235.0 million and $671.0 million over the prior year periods. On a per weighted average share basis, the net loss was $3.47 and $12.41 for the nine months ended September 30, 2023 and 2022, respectively.

Cash, cash equivalents and current financial assets totalled $3.2 billion as of September 30, 2023, compared to $2.2 billion as of December 31, 2022. The increase in cash and cash equivalents and current financial assets resulted primarily from the closing of a global offering of shares, including a U.S. offering, which resulted in the receipt of $1.2 billion in net proceeds in July 2023, partially offset by net cash flows used in operating activities.

EXPECTED 2024 FINANCIAL CALENDAR

February 29, 2024: FY 2023 financial results and business update
May 9, 2024: Q1 2024 financial results and business update
July 25, 2024: Q2 2024 financial results and business update
October 24, 2024: Q3 2024 financial results and business update
CONFERENCE CALL DETAILS
The third quarter 2023 financial results and business update will be discussed during a conference call and webcast presentation today at 1:30 pm CET/8:30 am ET. A webcast of the live call may be accessed on the Investors section of the argenx website at argenx.com/investors. A replay of the webcast will be available on the argenx website.

CytomX Therapeutics to Present Preclinical Data for Conditionally Activated Interferon Alpha-2b at the SITC 2023 Annual Meeting

On October 30 2023 CytomX Therapeutics, Inc. (Nasdaq: CTMX), a leader in the field of conditionally activated, localized biologics, reported that preclinical data supporting CX-801, its conditionally activated cytokine program, will be presented at the Society for Immunotherapy of Cancer (SITC) (Free SITC Whitepaper) Annual Meeting in San Diego, California (Press release, CytomX Therapeutics, OCT 30, 2023, View Source [SID1234636454]).

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Details for the poster presentation are as follows:
Presentation Title: Conditionally activated IFNa induces an inflammatory tumor microenvironment in preclinical models and increases efficacy in combination with checkpoint blockade
Abstract Number: 1064
Poster Hall A
Session Date and Time: November 4, 2023, 9:00 am – 8:30 pm PT

ImCheck To Present EVICTION-2 Data on ICT01 Combination With Low Dose
IL-2 In Patients with Advanced Solid Tumors at SITC Annual Meeting

On October 30, 2023 ImCheck Therapeutics reported that it will present updated data from its Phase I/IIa clinical trial EVICTION-2 in a poster presentation at the Society for Immunotherapy of Cancer (SITC) (Free SITC Whitepaper) 38th Annual Meeting 2023. In EVICTION-2, ImCheck’s lead program, ICT01, a humanized anti-BTN3A monoclonal antibody that selectively activates γ9δ2 T cells, is evaluated in combination with lose dose IL-2 on its ability to increase the number of γ9δ2 T cells and boost the anti-tumor immune response in patients with advanced-stage solid tumors (Press release, ImCheck Therapeutics, OCT 30, 2023, View Source [SID1234636453]). The conference will be held November 3-5 in San Diego, USA.

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Details of the poster presentation are:

Abstract title: "ICT01 plus Low Dose SC IL-2 Produces a Robust Anti-Tumor Immune Activation in Advanced Cancer Patients (EVICTION-2 Study)"
Session title: Clinical Trials in Progress
Abstract number: 715
Authors: Johann de Bono, Stéphane Champiat, Francois-Xavier Danlos, Martin Wermke, Volker Kunzmann, Aude De Gassart, Emmanuel Valentin, Marina Iché, Maelle Mairesse, Patrick Brune, Katrien Lemmens, Daniel Olive, Paul Frohna
Location: Exhibit Halls A and B1 – San Diego Convention Center
Date/Time: Friday, Nov. 3, 2023; 12:00–1:30 pm and 5:10–6:40 pm

Volastra Therapeutics Announces First Patient Dosed in Phase I/II Clinical Trial of VLS-1488, One in a Portfolio of Novel and Differentiated KIF18A Inhibitors

On October 30, 2023 Volastra Therapeutics, a discovery and clinical-stage cancer biotechnology company, reported the dosing of the first patient in a Phase I/II clinical trial evaluating VLS-1488 (Press release, Volastra Therapeutics, OCT 30, 2023, View Source [SID1234636451]). VLS-1488 and sovilnesib (formally AMG650) make up Volastra’s innovative clinical portfolio of differentiated KIF18A inhibitors specifically designed for the treatment of solid tumors characterized by high levels of chromosomal instability (CIN).

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The Phase I/II trial (NCT05902988) evaluates safety, tolerability and preliminary efficacy of VLS-1488 in patients with advanced tumors. The trial is a significant milestone in Volastra’s mission to help patients with these hard-to-treat cancers.

"In 2019, our team set out to understand the biology of chromosomal instability and discover new treatment approaches," said Charles Hugh-Jones M.D., FRCP, CEO at Volastra. "The ground-breaking work leading to this study has the potential to define the first-ever CIN-directed therapy."

KIF18A is a protein required by many tumor cells to divide and grow efficiently. It is not required by normal healthy cells to divide, allowing the selective killing of cancer cells. Volastra will deploy multiple exploratory biomarkers that measure CIN, including AI-based tissue imaging developed in partnership with Microsoft.

Dr. Pat LoRusso, D.O., Director of the Phase I Clinical Trial Unit at Yale commented, "Targeting chromosomal instability is a major opportunity for cancer therapy. Inhibiting KIF18A shows impressive data in pre-clinical models with high levels of CIN. We look forward to contributing to the clinical trial of this promising molecule."

Dr. Alexander Starodub, M.D., Ph.D., at The Christ Hospital Cancer Center in Cincinnati, Ohio dosed the first patient in this Phase 1 trial.

SELLAS Life Sciences Receives Fast Track Designation from FDA for SLS009 for Treatment of Relapsed/Refractory Peripheral T-cell Lymphomas

On October 30, 2023 SELLAS Life Sciences Group, Inc. (NASDAQ: SLS) ("SELLAS’’ or the "Company"), a late-stage clinical biopharmaceutical company focused on the development of novel therapies for a broad range of cancer indications, reported that the U.S. Food and Drug Administration (FDA) has granted Fast Track Designation to SLS009, its novel and highly selective CDK9 inhibitor, for the treatment of relapsed/refractory (r/r) Peripheral T-cell Lymphomas (PTCL) (Press release, Sellas Life Sciences, OCT 30, 2023, View Source [SID1234636450]). The Fast Track designation is intended to facilitate the development and review of drugs to treat serious conditions and fill an unmet medical need.

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"The FDA’s decision to grant SLS009 Fast Track designation signifies an important milestone towards developing a safe and effective treatment for PTCL, a group of aggressive and rare non-Hodgkin lymphomas, and underscores the urgent need for innovative therapies such as SLS009 that can significantly improve the outcome of PTCL patients," said Angelos Stergiou, MD, ScD h.c., President and Chief Executive Officer of SELLAS. "SLS009 has demonstrated very promising clinical responses in PTCL patients in the recently completed dose-escalation portion of the Phase 1 trial in relapsed/refractory hematological malignancies and with the Fast Track designation we are poised to accelerate its development. We are committed to working closely with the FDA and our partner GenFleet Therapeutics to develop this promising treatment for patients in need."

SLS009 demonstrated favorable safety/tolerability and promising clinical efficacy in the recently completed dose-escalation portion of the Phase 1 trial in r/r hematological malignancies. Complete or partial responses were observed in acute myeloid leukemia and lymphoma patients among which four out of eleven patients with PTCL (36.4%) achieved clinical responses including one in continuous treatment for over 56 weeks. The current standard of care for PTCL, belinostat, approved for r/r PTCL, showed in its pivotal Phase 2 study a 25.8% response rate in a similar patient population to that in the SLS009 Phase 1 clinical trial. An open-label, single-arm Phase 1b/2 trial of SLS009 (known as GFH009 in China) to evaluate safety and efficacy in r/r PTCL, at the recommended phase 2 dose of 100 mg once per week, is ongoing in China and, based on the results, may serve as a registrational study.

This initial PTCL study, which will enroll up to 95 patients, is fully funded by GenFleet Therapeutics (Shanghai) Inc. The Company is also actively pursuing potential Breakthrough Therapy designation from the FDA for SLS009 for the treatment of r/r PTCL and has a scheduled meeting in the fourth quarter of 2023 to discuss with the FDA.

Fast Track is a process designed by the FDA to facilitate and expedite the development of investigational treatments that demonstrate a potential to address unmet medical needs in serious or life-threatening conditions. Programs with Fast Track designation can benefit from early and more frequent interactions with the FDA to discuss the candidate’s development plan in addition to a rolling submission of the marketing application. Therapeutic candidates with Fast Track designation may also be eligible for priority review and accelerated approval if supported by clinical data.